Join us at Health Research Day — June 6th at Canton Waterfront Park, Baltimore!   Learn More →
← Back to all trials
Active Not Recruiting NCT05112237

Natural History Study in Pediatric Patients With MYBPC3 Mutation-associated Cardiomyopathy

Conditions: Cardiomyopathy

Sex: All
Ages: 0 Years – 18 Years
Healthy volunteers: No
Enrollment: 200
Sponsor: Tenaya Therapeutics

Location: Arkansas Children's Hospital Little Rock Arkansas

Summary

The objective of this study is to collect information on patients with cardiomyopathy (CM) due to mutations in the MYBPC3 gene, to evaluate their disease course, burden of illness, risk factors for this disease, and the quality of life (QoL). This study will also collect information on treatments, procedures and outcome in infants and children up to 18 yrs who have this mutation.

Eligibility Criteria

Retrospective Inclusion Criteria: * Data is available for patient \

Interested in this study? View the official listing for contact and enrollment details.

View on ClinicalTrials.gov

Source: ClinicalTrials.gov (NCT05112237). StuddyBuddy aggregates publicly available trial information.