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Active Not Recruiting
NCT03974113
Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B
Conditions: Hemophilia
Sex: Male
Ages: 1 Year – 11 Years
Healthy volunteers: No
Phase: PHASE2, PHASE3
Enrollment: 32
Sponsor: Genzyme, a Sanofi Company
Location: Children's Hospital Los Angeles Site Number : 8400002 Los Angeles California
Summary
Primary Objective:
\- To confirm appropriate dose levels of fitusiran when administered to male pediatric participants (ages 1 to \
Eligibility Criteria
Inclusion Criteria:
* Male, aged 1 to \
Source: ClinicalTrials.gov (NCT03974113). StuddyBuddy aggregates publicly available trial information.