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Recruiting NCT03291223

Gaucher Disease Outcome Survey (GOS)

Conditions: Gaucher Disease

Sex: All
Healthy volunteers: No
Enrollment: 1257
Sponsor: Shire

Location: Central Contact Lexington Massachusetts

Summary

The Gaucher Outcomes Survey (GOS) is an ongoing observational, international, multi-center, long-term Registry of Patients with Gaucher Disease irrespective of their treatment status or type of treatment received. No experimental intervention is involved. Patients undergo clinical assessments and receive care as determined by the patients' treating physician. The objectives of the registry include to evaluate the safety and long-term effectiveness of velaglucerase alfa, to characterize patients receiving velaglucerase alfa or other Gaucher Disease-specific treatments, to gain a better understanding of the natural history of GD and to serve as a database for evidence-based management of Gaucher Disease over time in real-life clinical practice.

Eligibility Criteria

Inclusion Criteria: * Patients of any age or gender with confirmed diagnosis (biochemical and/or genetic) of Gaucher disease * Signed and dated written informed consent from the patient or, for patients aged \

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View on ClinicalTrials.gov

Source: ClinicalTrials.gov (NCT03291223). StuddyBuddy aggregates publicly available trial information.