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Recruiting
NCT03190837
A Long-term Follow-up Study of Gaucher Disease
Conditions: Gaucher Disease
Sex: All
Enrollment: 200
Sponsor: Duke University
Location: Duke University Medical Center Durham North Carolina
Summary
The study aims are to: a) identify the long-term natural history of Gaucher disease, b) evaluate long-term treatment efficacy of enzyme replacement therapy (ERT) and substrate reduction therapy (SRT), and c) identify potential long-term complications of this disorder. These aims will be accomplished through long-term record review of individuals with all three types of Gaucher disease.
Eligibility Criteria
Inclusion Criteria:
* Diagnosis of Gaucher Disease
Exclusion Criteria:
* Not meeting Inclusion criteria
Source: ClinicalTrials.gov (NCT03190837). StuddyBuddy aggregates publicly available trial information.
